We don’t follow footsteps. We create the path.

Spark® Therapeutics at the Bulletin Building in Philadelphia

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We don’t follow footsteps. We create the path.

Our mission at Spark® Therapeutics is to unlock the power of gene therapy to accelerate healthcare transformation. We have built a fully integrated company, combining our proprietary adeno-associated viral (AAV) gene therapy platform with excellence in R&D, manufacturing and commercial operations. Find out more about how we strive to turn genes into medicines for patients with inherited diseases, including inherited retinal diseases (IRDs), liver-directed diseases such as hemophilia, and neurodegenerative diseases.

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