Creating
a new path

News & events

News updates
Learn more about multiple updates for investigational voretigene neparvovec

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JPM 2017
Missed our JPM presentation? Tune into the webcast here

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ID YOUR IRD
Genetic testing now available to eligible patients with certain IRDs through the new Spark initiative, ID YOUR IRD

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Meet our inspiration
Meet Eric Hartman, an accomplished Impressionist-style painter, living with choroideremia

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We don’t follow footsteps. We create the path.

Our mission at Spark Therapeutics is to challenge the inevitability of genetic disease by discovering, developing and delivering potential treatments in ways unimaginable—until now. We have built a fully integrated company, combining our proprietary adeno-associated viral (AAV) gene therapy platform with excellence in R&D, manufacturing and commercial operations. Find out more about how we strive to turn genes into medicines for patients with inherited diseases, including inherited retinal diseases (IRDs), liver-mediated diseases such as hemophilia, and neurodegenerative diseases.

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