We don’t follow footsteps.
We create the path.

News & events

Gene Therapy Approval
FDA has approved our gene therapy product

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New Posting on Health Affairs Magazine Blog: 
Advancing Gene Therapies Through Value-Based Payment Reform

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59th ASH Annual Meeting
Spark Therapeutics presents updated hemophilia A and B data at the 2017 American Society of Hematology Annual Meeting

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Hemophilia B data published in NEJM
The New England Journal of Medicine published data from Spark’s Phase 1/2 study of investigational SPK-9001

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We don’t follow footsteps. We create the path.

Our mission at Spark Therapeutics is to challenge the inevitability of genetic disease by discovering, developing and delivering potential treatments in ways unimaginable—until now. We have built a fully integrated company, combining our proprietary adeno-associated viral (AAV) gene therapy platform with excellence in R&D, manufacturing and commercial operations. Find out more about how we strive to turn genes into medicines for patients with inherited diseases, including inherited retinal diseases (IRDs), liver-mediated diseases such as hemophilia, and neurodegenerative diseases.

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